Status | Study |
Enrolling by invitation |
Study Name: PoC Study to Assess Activity and Safety of SMT C1100 (Ezutromid) in Boys With DMD Condition: Duchenne Muscular Dystrophy Date: 2016-07-27 Interventions: Drug: ezutromid oral suspension Other Name: SMTC1100 |
Recruiting |
Study Name: Characterization of Clinical Skeletal and Cardiac Impairment in Carriers of DMD and BMD Condition: Duchenne Muscular Dystrophy Becker Muscul Date: 2016-07-25 Interventions: Genetic: Genetic characterization Longitudinal prospective observational study |
Recruiting |
Study Name: Validating Cardiac MRI Biomarkers and Genotype-Phenotype Correlations for DMD Condition: Muscular Dystrophy, Duchenne Date: 2016-07-13 Interventions: Other: Cardiac MRI with contrast |
Not yet recruiting |
Study Name: Treatment Effect of Tamoxifen on Patients With DMD Condition: Duchenne Muscular Dystrophy Date: 2016-06-22 Interventions: Drug: Tamoxifen |
Recruiting |
Study Name: Acceptance and Commitment Therapy for Muscle Disease Condition: Muscle Diseases Date: 2016-06-20 Interventions: Behavioral: Acceptance and Commitment Therapy (ACT) Acceptance and Commitment Therapy (ACT) is a form of |
Recruiting |
Study Name: A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucocorticoid Steroids Condition: Duchenne Muscular Dystrophy (DMD) Date: 2016-06-17 Interventions: Drug: Idebenone 150 mg film-coated tablets |
Active, not recruiting |
Study Name: Study of Ataluren in ≥2 to <5 Year-Old Males With Duchenne Muscular Dystrophy Condition: Duchenne Muscular Dystrophy Date: 2016-06-16 Interventions: Drug: Ataluren Ataluren Other Names: |
Recruiting |
Study Name: Study to Assess the Safety, Tolerability and PK Response and Explore the PD Response Following 4 Weekly SC Injections of PB1046 in Subjects With Stable Heart Failure With Reduced Ejection Fraction (HFrEF) Condition: Heart Failure Date: 2016-06-08 Interventions: Drug: PB1046 Injection Four we |
Recruiting |
Study Name: Muscle Oxygenation in Effort in Neuromuscular Diseases Condition: Neuromuscular Diseases Date: 2016-05-24 Interventions: Other: muscle oxygenation Subjects will be invited to perform an isokinetic effort of the knee extensors |
Recruiting |
Study Name: Outcome Measures in Duchenne Muscular Dystrophy: A Natural History Study Condition: Duchenne Muscular Dystrophy Date: 2016-05-19 Interventions: Other: Set of assessment tools |